1R01HL177642-01 (PI: ElMallah)
Sponsor: IH/NICHD
Title: Alveolar injury and repair in Pompe Disease
This project will examine the impact of lung injury on Pompe disease and the ability of Pompe disease alveolar cells to repair and regenerate. We will also examine the impact of enzyme replacement therapy and gene therapy on the pathology in the alveolar cells.
Pfizer-GTF (PI: ElMallah, Postdoc: McCall)
Sponsor: Pfizer/NCBiotech
Title: “Distinguished Postdoctoral Fellowship in Gene Therapy”
This competitive award funds two-year fellowships that enable early career scientists to conduct research in the laboratories of gene therapy-related investigators at any North Carolina university.
1R01HD099486-01 (PI: ElMallah)
Sponsor: NIH/NICHD
Title: “Targeted gene therapy for Pompe disease”
An investigation of smooth muscle pathology in Pompe disease and the impact of ERT and AAV gene therapy on smooth muscle pathology and respiratory pathology in the Pompe disease mouse model.
Sarepta Research Grant (PI: ElMallah)
Sponsor: Sarepta
Title: “Novel murine models of DMD”
This grant provides support to study respiratory function in novel DMD mouse models and the impact of phosphorodiamidate morpholino oligomers (PPMOs) on respiratory function and pathology.
1R21NS112781-01A1 (PI: ElMallah)
