Pfizer-GTF (PI: ElMallah, Postdoc: McCall)

Sponsor: Pfizer/NCBiotech

Title: “Distinguished Postdoctoral Fellowship in Gene Therapy”

This competitive award funds two-year fellowships that enable early career scientists to conduct research in the laboratories of gene therapy-related investigators at any North Carolina university.

1R01HD099486-01 (PI: ElMallah)

Sponsor: NIH/NICHD

Title: “Targeted gene therapy for Pompe disease”

An investigation of smooth muscle pathology in Pompe disease and the impact of ERT and AAV gene therapy on smooth muscle pathology and respiratory pathology in the Pompe disease mouse model.

Sarepta Research Grant (PI: ElMallah)

Sponsor: Sarepta

Title: “Novel murine models of DMD”

This grant provides support to study respiratory function in novel DMD mouse models and the impact of phosphorodiamidate morpholino oligomers (PPMOs) on respiratory function and pathology.

1R21NS112781-01A1 (PI: ElMallah)

Sponsor: NIH/NINDS

Title: “Respiratory Dysfunction in an Optineurin Knock Out ALS Mouse Model”

This grant examines the impact of intermittent hypoxia on neuroplasticity in optineurin deficient mice – an animal model of ALS.